Content tagged "gene therapy":

Shefali Setia Verma, PhD
Assistant Professor of Pathology and Laboratory Medicine
Perelman School of Medicine at the University of Pennsylvania
Beverly L. Davidson, PhD

Professor of Pathology and Laboratory Medicine
Professor of Genetics
Perelman School of Medicine at the University of Pennsylvania 

Chief Scientific Strategy Officer 
Director, Raymond G. Perelman Center for Cellular and Molecular Therapeutics
Katherine A High Presidential Scholar Endowed Chair in Cell and Gene Therapy
Children’s Hospital of Philadelphia (CHOP)

Top 50 Most Influential People in Vaccines

August 31, 2014

Dr. David Weiner is among the 2014 Top 50 "Most Influential People in Vaccines." Dr. Weiner’s research in the area of Molecular Immunology has focused extensively on the development of gene-based vaccines and immune therapies.

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Gene Therapy Approach for New Treatment of Rare Disease MPS I

August 28, 2014

The lab of James M. Wilson, MD, PhD, director of the Penn Gene Therapy Program, has published a proof-of-principle animal study that reduces harmful accumulation of proteins in a rare lysosomal storage disease through direct gene therapy.

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Bruce L. Levine, PhD

Barbara and Edward Netter Professor in Cancer Gene Therapy
Perelman School of Medicine at the University of Pennsylvania

Founding Director, Clinical Cell and Vaccine Production Facility (CVPF)

Vijay Bhoj, MD, PhD
Assistant Professor of Pathology and Laboratory Medicine at the Hospital of the University of Pennsylvania
Perelman School of Medicine at the University of Pennsylvania

Gene Therapy Pioneers

November 19, 2013

The peer-reviewed journal Human Gene Therapy is celebrating its 25th anniversary in 2014 by publishing a series of Perspectives by top researchers in the field of cell and gene therapy. Five "Pioneer" scientists from the Perelman School of Medicine at the University of Pennsylvania are among the 21 investigators who will be honored throughout the next 12 months.

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Endowed Professorship in Cancer Gene Therapy

September 30, 2013

A $1.5 million gift to the University of Pennsylvania has established the Barbara and Edward Netter Associate Professorship in Cancer Gene Therapy at the Abramson Cancer Center. Bruce Levine, PhD, a faculty member in the department of Pathology and Laboratory Medicine in the Perelman School of Medicine and the director of the Clinical Cell and Vaccine Production Facility, has been appointed to the Barbara and Edward Netter Associate Professor in Cancer Gene Therapy.

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New Gene Therapy Research Shows Broad Protection in Animal Models Against Pandemic Flu Strains, Including the Deadly 1918 Spanish Influenza

May 29, 2013

Investigators in the Gene Therapy Program, Department of Pathology and Laboratory Medicine, directed by James M. Wilson, MD, PhD, have demonstrated that a single dose of an adeno-associated virus (AAV) expressing a broadly neutralizing flu antibody into the nasal passages of mice and ferrets gives them complete protection and substantial reductions in flu replication when exposed to lethal strains of H5N1 and H1N1 flu virus. These strains were isolated from samples associated from historic human pandemics – one from the infamous 1918 flu pandemic and another from 2009.

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